Results from Phase 3 ENERGIZE-T Study of Mitapivat in Transfusion-dependent Thalassemia will be Presented in Oral Session –– Tebapivat Phase 1 ...

Doctors stress the importance of awareness and testing for thalassemia, a genetic blood disorder affecting children, as cases continue to rise due to lack of information and government programs.

Patients with transfusion-dependent β-thalassemia experienced 14.8 hospitalizations annually, according to the findings.

My son won’t need monthly hospital trips anymore.""I’m happy to be better and grateful to the doctors," said Vuong, touching ...

In-depth interviews and an online survey found support for gene therapy as a treatment for inherited blood disorders, but ...

Mumbai’s blood banks face critical shortages during Diwali as donation drives decrease. Children with thalassemia and ...

BAKU, Azerbaijan, October 31. Mehriban Aliyeva, First Vice-President of the Republic of Azerbaijan and President of the ...

Doctors & patients confirm acute shortage of the drug in hospitals, even as manufacturer Novartis maintains there is no ...

Azerbaijan's First Vice-President and the President of the Heydar Aliyev Foundation, Mehriban Aliyeva, visited the ...

Beam Therapeutics enrolls 35 patients in BEACON trial for BEAM-101 in sickle cell disease, with promising early safety and ...

CASGEVY™ approved for the treatment of patients 12 years of age and older with sickle cell disease (SCD) and transfusion-dependent beta ...

Q3 2024 Earnings Conference Call October 31, 2024 8:00 AM ET. Company Participants. Chris Taylor - Vice President, Investor Relations and ...