Agios is hoping for a broad label in thalassemia, covering both alpha and beta subtypes regardless ... they sold their oncology business) for the treatment of malignant brain tumors.

Conditions such as alpha thalassemia major, where the fetus cannot produce adequate red blood cells ... and addressing any ...

This achievement represents a major advancement in the treatment of genetic disorders, offering a potential permanent solution to thalassemia major, a severe blood disorder caused by genetic mutations ...

RIYADH: Saudi Arabia’s King Abdulaziz Medical City in Riyadh (KAMC-RD) has successfully treated a teenager’s thalassemia employing Casgevy gene therapy through clustered regularly interspaced ...

CRISPR Therapeutics' stock may seem boring due to slow FDA trial and rollout process, but it's a strong long-term investment.

My name is Ipshita kayasta and I am raising funds for my daughter, Ipshita kayasta who is suffering from Thalassemia major and is undergoing treatment at SRCC Children's Hospital, Mumbai. The family ...

World Thalassemia Day was observed on Wednesday. This year’s theme is “Empowering Lives, Embracing Progress: Equitable and Accessible Thalassemia Treatment for All’’. International Thalassemia Day is ...

Agios Pharmaceuticals has announced that the US Food and Drug Administration (FDA) has granted orphan drug designation (ODD) ...