Conditions such as alpha thalassemia major, where the fetus cannot produce adequate red blood cells ... and addressing any ...

Crispr Therapeutics 40% share in Casgevy could result in revenue annual between $1.2 billion and $2.8 billion towards the end ...

Mitapivat, the company’s lead PK activator, was previously granted FDA orphan drug designation for the treatment of PK deficiency, thalassemia, and sickle cell disease. Tebapivat is not approved for ...

Elon Musk has amplified a theory that only "alpha males" can be trusted to make good decisions, and should therefore be the ones to participate in democracy. On Monday the billionaire entrepreneur ...

Some Gen Alpha kids are into minimalism and decluttering. They value sustainability and quality thanks to better environmental awareness, experts said. They are still likely to be a generation of ...

A doctor still practising at the age of 87 was struck off after giving two children unconventional treatments. Dr Jean Monro, who qualified in 1960, prescribed unlicensed medication to a girl and ...

Two Perth patients with advanced melanoma have become the first in Australia to try a new type of cancer treatment. The treatment included standard immunotherapy, followed by surgery, high-dose ...

I’d put off seeking help for years, scarred by bad experiences as an adolescent that involved too many drugs, punitive treatments, and clueless counselors. Finally, at 25, I was here ...

This achievement represents a major advancement in the treatment of genetic disorders, offering a potential permanent solution to thalassemia major, a severe blood disorder caused by genetic mutations ...

It is important for your medical team to identify the cause because macrocytic anemia can improve with the appropriate treatment. Macrocytic anemia is characterized by macrocytosis, which is large red ...