BioMarin Pharma has its landmark first approval for Roctavian – the first for a haemophilia gene therapy – and will now have to see if that can convert that into a viable business in Europe.

Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent after a single infusion of gene therapy, according to the new results of an ...

Summary: Researchers have developed the first 3D map of gene regulation in the human brain, offering insights into how early brain development influences lifelong mental health. This map, focusing on ...

HGNC is responsible for approving unique symbols and names for human loci to allow unambiguous scientific communication.

NGS provides more information than single-gene testing and can be used to deliver personalised, targeted treatment, but isn’t being offered to the “tens of thousands of people across Europe ...

Instead, arm yourself with the stats seen in these cool maps of Europe. After all, who knows what geography questions they'll help answer at the next trivia night? Although not as common as in the ...

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The "Nucleic Acid Therapeutics CDMO Market Size, Share & Trends Analysis, 2024-2030" report has been added to ...

08, 2024 (GLOBE NEWSWIRE) -- Somagenetix AG, a pioneering biotech company dedicated to revolutionizing gene therapy for phagocyte disorders ... About Vi Partners Vi Partners is one of the oldest VC ...

This milestone represents significant progress in Ferring’s manufacturing capabilities to meet anticipated growth in demand for Adstiladrin ® (nadofaragene firadenovec-vncg), a gene therapy for people ...