Sangamo said it plans to explore all options to commercialise the asset, including seeking a potential new collaboration ...

Gene therapy is referred to as a medical technique that involves modifying or manipulating genes to treat or prevent disease.

Novartis NVS announced positive top-line results from the late-stage STEER study on experimental candidate intrathecal ...

The newly approved medicines in 2024 from Massachusetts companies range from a schizophrenia drug to a gene therapy for ...

GT-0002X is under clinical development by Gene Therapy Research Institution and currently in Phase II for Parkinson's Disease.

Sangamo Therapeutics Inc. fell as much as 67% in extended trading after Pfizer Inc. ended its partnership to develop a new ...

Sangamo Therapeutics, Inc. (NASDAQ:SGMO) regained the development and commercialization rights to giroctocogene fitelparvovec ...

Novartis AG said a new experimental medicine improved motor function in children with a form of spinal muscular atrophy, the ...

From a pig kidney transplant to restoring genetic deafness, 2024 was a year full of medical breakthroughs. The breakthroughs ...

An experimental gene therapy might one day give people with heart failure a new lease on life. The therapy prompted the pigs’ ...

The FDA approved an injectable version of Opdivo, a cancer drug by Bristol Myers Squibb. Axsome plans to seek approval for ...

After two recent deaths in gene therapy clinical trials, the industry needs to be more open to sharing information to protect ...