The patent highlights the versatility of the nucleic acid molecule, which can be delivered via viral vectors, such as lentiviral vectors, thereby expanding its potential applications in therapeutic ...
Following a comprehensive review of its operations, bluebird bio, Inc. (Nasdaq: BLUE) today announced that the Company is implementing a restructuring intended to optimize the Company’s cost structure ...
Researchers tested a preclinical model for an experimental gene therapy designed to treat multiple sulfatase deficiency (MSD), a disorder that affects the brain, lungs, skin, and skeleton with no ...