With new approvals on the horizon and the closely watched Casgevy launch picking up steam in sickle cell disease and beta ...

CASGEVY™ approved for the treatment of patients 12 years of age and older with sickle cell disease (SCD) and ...

Doctors stress the importance of awareness and testing for thalassemia, a genetic blood disorder affecting children, as cases continue to rise due to lack of information and government programs.

My son won’t need monthly hospital trips anymore.""I’m happy to be better and grateful to the doctors," said Vuong, touching ...

Beam Therapeutics enrolls 35 patients in BEACON trial for BEAM-101 in sickle cell disease, with promising early safety and ...

In-depth interviews and an online survey found support for gene therapy as a treatment for inherited blood disorders, but ...

Results from Phase 3 ENERGIZE-T Study of Mitapivat in Transfusion-dependent Thalassemia will be Presented in Oral Session –– Tebapivat Phase 1 ...

Patients with transfusion-dependent β-thalassemia experienced 14.8 hospitalizations annually, according to the findings.

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Achieved in vivo preclinical proof of concept of HBG1/2 editing in hematopoietic stem and progenitor cells (HSPCs) using Editas Medicine’s ...

Azerbaijan's First Vice-President and the President of the Heydar Aliyev Foundation, Mehriban Aliyeva, visited the ...

BAKU, Azerbaijan, October 31. Mehriban Aliyeva, First Vice-President of the Republic of Azerbaijan and President of the ...