To model mitapivat's potential in thalassemia, I will use aggressive ... Agios after they sold their oncology business) for the treatment of malignant brain tumors. This is expected to increase ...
For those with beta-0 thalassemia, their condition is usually more severe, while beta+ thalassemia tends to be milder. Treatment and Care The main goal of treatment is to reduce painful episodes and ...
CRISPR Therapeutics' first therapy is called Casgevy. It treats sickle cell disease (SCD) and beta thalassemia, both rare inherited illnesses that affect the function of a person's red blood cells. It ...