Angus Powell, three, carries a rare mutation in the CRELD1 gene. The disorder it causes has now been named: Jeffries-Lakhani ...

Gene therapy is referred to as a medical technique that involves modifying or manipulating genes to treat or prevent disease.

In individuals undergoing repeated blood exchanges or transfusions, however, the amount of iron introduced into their bodies ...

This phase 1–2, randomised, double-blind, placebo-controlled trial enrolled 130 patients aged 18 or older with confirmed ...

Check out this year's top coverage from The Academy of Managed Care Pharmacy (AMCP) Nexus 2024 meeting, which included ...

Chad Stevens traveled from Idaho to Omaha's Nebraska Medical Center, where he became the hospital's first patient to receive ...

A recent study from Johns Hopkins Medicine has found that a drug originally developed to treat Alzheimer’s disease, ...

Human beings are a bit of a puzzle. There’s a paradoxical desire for connection with others while also staying unique. On the ...

A groundbreaking study has shown that exagamglogene autotemcel (exa-cel), a CRISPR-based gene therapy, can effectively ...

In fact, it wasn’t until 2016 that Seacole became the first Black woman to be honoured with a statue in the UK, symbolising ...

Gene therapies are revolutionizing treatment for hemophilia A and sickle cell disease; however, they are saddled with hefty ...