mRNA-3705 is under development for the treatment of methylmalonic acidemia (MMA). It acts by targeting methylmalonyl CoA mutase (MUT) enzyme. The therapeutic candidate comprises of messenger RNA (mRNA ...

Methylmalonic acidemia (MMA) is a rare and potentially fatal genetic disorder that affects metabolism and multiple body systems that affects about one in 100,000 infants. It's caused by a genetic ...

These are Maple Syrup Urine Disease, Methylmalonic Acidemia/Propionic Acidemia, Galactosemia, Phenylketonuria, Gaucher Disease, Pompe Disease, Fabry Disease, MPS II (Hunter Syndrome), MPS IV ...

Philippine Health Insurance Corporation (PhilHealth) announced on Monday new benefit packages covering various illnesses as part of its commitment in the implementation of the Universal Health Care ...

DOH noted that the improved benefits endorsed for Board approval include a package for acute myocardial infarction (AMI) or heart attacks across the continuum of care; ten rare diseases, including ...

The endorsed benefit packages for approval include a package for acute myocardial infarction or heart attacks across the continuum of care and a package for each of these rare diseases – Maple Syrup ...